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10 Sep 2019 |
Passage Bio Announces New Gene Therapy Development Program for Patients with Charcot-Marie-Tooth Neuropathy Type 2A
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10 Sep 2019 |
Translate Bio Announces Pipeline Program Update
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05 Sep 2019 |
Rocket Pharmaceuticals Announces First Patient Treated in Phase 1/2 Registrational Trial of RP-L201 for LAD-I
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05 Sep 2019 |
Krystal Biotech Announces Initiation of Phase 1/2 Study of KB105 in Transglutaminase-1 (“TGM1”) Deficient Autosomal Recessive Congenital Ichthyosis (“ARCI”)
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05 Sep 2019 |
Nkarta Therapeutics Raises $114 Million in Series B Financing to Advance Multiple Programs into Clinical Trials
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04 Sep 2019 |
Ultragenyx Announces Positive Data from Phase 1/2 Study of DTX401 Gene Therapy in Glycogen Storage Disease Type Ia
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02 Sep 2019 |
The Medicines Company Presents Results from ORION-11, First Phase 3 Trial of Inclisiran, Showing Durable and Potent Lowering of LDL-C with Twice-Yearly Dosing
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29 Aug 2019 |
Immunicum AB (publ) Announces Positive Phase II MERECA Topline Results Including Complete Tumor Responses in Metastatic Renal Cell Carcinoma Patients
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29 Aug 2019 |
Arrowhead Collaborator Janssen Begins REEF-1 Phase 2b Combination Study in Patients with Chronic Hepatitis B Infection
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27 Aug 2019 |
The Medicines Company Announces Positive Topline Results from First Pivotal Phase 3 Trial of Inclisiran
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21 Aug 2019 |
NKMax America Initiates Phase I Clinical Trial of SNK in Patients with Psoriasis in Mexico
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20 Aug 2019 |
Synlogic Discontinues Development of SYNB1020 to Treat Hyperammonemia
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20 Aug 2019 |
Sarepta Therapeutics Receives Complete Response Letter from the US Food and Drug Administration for Golodirsen New Drug Application
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16 Aug 2019 |
City of Hope Now Enrolling Patients for First-in-Human T Cell Trial for HPV-Associated Cancers
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14 Aug 2019 |
NKMax America Doses First Subject in Phase I Trial of SNK in Patients with Refractory Cancer
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14 Aug 2019 |
Mallinckrodt Announces Publication of Results of Phase 1b Clinical Trial of StrataGraft® Regenerative Tissue in Burns
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14 Aug 2019 |
Renovacor Closes $11 Million Series A Financing to Advance First Gene Therapy for a Rare Cardiovascular Disease
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13 Aug 2019 |
ProQR Announces Clearance of IND to Start Clinical Trial of QR-1123 in Patients with Autosomal Dominant Retinitis Pigmentosa (adRP)
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12 Aug 2019 |
TScan Therapeutics Announces Pioneering Publication in Scientific Journal Cell Describing New Methods to Identify Targets for T Cell Receptor Immunotherapy
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08 Aug 2019 |
Arrowhead Pharmaceuticals Doses First Patient in SEQUOIA Phase 2/3 Study of ARO-AAT for Treatment of Alpha-1 Liver Disease
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07 Aug 2019 |
Moderna Provides Business Updates and Reports Second Quarter 2019 Financial Results
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07 Aug 2019 |
Akcea and Ionis Report Top-line Results from the BROADEN Study with WAYLIVRA® (volanesorsen) in Patients with Familial Partial Lipodystrophy
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07 Aug 2019 |
Novartis stands behind Zolgensma® (onasemnogene abeparvovec-xioi) for the treatment of children less than 2 years of age with spinal muscular atrophy
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06 Aug 2019 |
Evelo Biosciences Reports Positive EDP1815 Interim Clinical Data in Psoriasis Patients at Low Dose in Ongoing Phase 1b Trial
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06 Aug 2019 |
MOLOGEN AG Announces Top Line Data of Pivotal IMPALA Study in Metastatic Colorectal Cancer
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