Bobcat mRNATM technology is a novel linear mRNA platform able to encode large proteins
Data showed restoration of muscular function in DMD mouse model
BALTIMORE, MD, USA I March 04, 2024 I Elixirgen Therapeutics, Inc., a clinical-stage biotechnology company focused on the discovery, development and commercialization of therapies using its mRNA platforms, today presented preclinical data on its proprietary Bobcat mRNATM technology in a poster presentation at the 2024 Muscular Dystrophy Association (MDA) Clinical & Scientific Conference taking place March 3-6, 2024, in Orlando, Florida. Bobcat mRNATM is designed to deliver large protein payloads (over 13 kb), and results show that a Bobcat mRNATM encoding a full-length dystrophin protein can restore muscular function in a mouse model for Duchenne muscular dystrophy (DMD).
“We’re excited to be presenting these promising data on our novel Bobcat mRNATM technology. Dystrophin, the largest known human gene, is mutated in DMD, which is a rare disease that causes progressive muscle weakness and atrophy,” said Aki Ko, Co-Founder and Chief Executive Officer of Elixirgen Therapeutics. “Our Bobcat mRNATM full-length dystrophin approach may be complementary to others currently approved or in development, or may even mitigate some of their issues. We’re pleased to add the Bobcat mRNATM technology to our pipeline of RNA technologies and look forward to sharing updates in the months ahead.”
Presentation Title: Development of mRNA Therapeutic Delivering Full-length Dystrophin for Duchenne Muscular Dystrophy
Poster Number: T428
About Elixirgen Therapeutics, Inc.
Elixirgen Therapeutics, Inc. is a clinical-stage biotechnology company focused on the discovery, development and commercialization of therapies using its mRNA platforms and ZSCAN4 technology. The company has one ongoing (NCT04211714) and one completed (NCT04863131) Phase 1/2 clinical trial. For more information, visit ElixirgenTx.com.
SOURCE: Elixirgen Therapeutics
Post Views: 393
Bobcat mRNATM technology is a novel linear mRNA platform able to encode large proteins
Data showed restoration of muscular function in DMD mouse model
BALTIMORE, MD, USA I March 04, 2024 I Elixirgen Therapeutics, Inc., a clinical-stage biotechnology company focused on the discovery, development and commercialization of therapies using its mRNA platforms, today presented preclinical data on its proprietary Bobcat mRNATM technology in a poster presentation at the 2024 Muscular Dystrophy Association (MDA) Clinical & Scientific Conference taking place March 3-6, 2024, in Orlando, Florida. Bobcat mRNATM is designed to deliver large protein payloads (over 13 kb), and results show that a Bobcat mRNATM encoding a full-length dystrophin protein can restore muscular function in a mouse model for Duchenne muscular dystrophy (DMD).
“We’re excited to be presenting these promising data on our novel Bobcat mRNATM technology. Dystrophin, the largest known human gene, is mutated in DMD, which is a rare disease that causes progressive muscle weakness and atrophy,” said Aki Ko, Co-Founder and Chief Executive Officer of Elixirgen Therapeutics. “Our Bobcat mRNATM full-length dystrophin approach may be complementary to others currently approved or in development, or may even mitigate some of their issues. We’re pleased to add the Bobcat mRNATM technology to our pipeline of RNA technologies and look forward to sharing updates in the months ahead.”
Presentation Title: Development of mRNA Therapeutic Delivering Full-length Dystrophin for Duchenne Muscular Dystrophy
Poster Number: T428
About Elixirgen Therapeutics, Inc.
Elixirgen Therapeutics, Inc. is a clinical-stage biotechnology company focused on the discovery, development and commercialization of therapies using its mRNA platforms and ZSCAN4 technology. The company has one ongoing (NCT04211714) and one completed (NCT04863131) Phase 1/2 clinical trial. For more information, visit ElixirgenTx.com.
SOURCE: Elixirgen Therapeutics
Post Views: 393